Interventional trials in ENR-RND – Ataxia and HSP – ERN-RND | European Reference Network on Rare Neurological Diseases

Disease	Treatment	Center	Contact	Key information
Friedreich Ataxia	Vatiquinone	Paris Brain Institute - Pitié Sapetriere University Hospital Paris France	" style="color: #009900;">Contact
SCA3	Trehalose	Hospital Clinic Barcelona Spain	">Contact	Patient recruitment temporarily halted
Hereditary Spastic Paraplegia		University Hospital Innsbruck Austria	">Contact	not yet registered
SCA1 and SCA3	Antisense oligonucleotide, intrathecally injected; phase1/2A	Radboud university medical center Nijmegen Netherlands	">Contact	Recruitment of Dutch patients only
Friedreich Ataxia	Omaveloxolon	Fondazione IRCCS Istituto Neurologico Carlo Besta Milan Italy
Friedreich Ataxia	Phase 3	Bambino Gesù — Children's Hospital Rome Italy
Friedreich Ataxia	Vatiquinone	Bambino Gesù — Research Hospital Rome Italy	">Rene Gallegos - Associate Director Clinical Operations MOVE-FA ">Briana Johnson - Manager Clinical Operations PTC743-003e
FRDA	N/A	TUH Dublin Ireland	">Contact
SCA and CANVAS	rTMS	University Hospital Bonn Germany	">Contact
MSA	i.v. TAK-341	DZNE Bonn Germany	" style="color: #007acc;">Contact
SCA1, SCA3, Huntington	ASO	DZNE Bonn Germany	">Contact
SCA3	Intrathecal ASO	DZNE Bonn Germany	">Contact	trial stopped
Friedreich Ataxia	Omaveloxolon	Center for rare movement disorders Innsbruck Austria	">Contact