Interventional trials in ENR-RND – Ataxia and HSP

DiseaseTreatmentCenterContactKey information
Friedreich AtaxiaVatiquinoneParis Brain Institute - Pitié Sapetriere University Hospital Paris France" style="color: #009900;">Contact
SCA3TrehaloseHospital Clinic Barcelona Spain">ContactPatient recruitment temporarily halted
Hereditary Spastic ParaplegiaUniversity Hospital Innsbruck Austria">Contactnot yet registered
SCA1 and SCA3Antisense oligonucleotide, intrathecally injected; phase1/2ARadboud university medical center Nijmegen Netherlands">ContactRecruitment of Dutch patients only
Friedreich AtaxiaOmaveloxolonFondazione IRCCS Istituto Neurologico Carlo Besta Milan Italy
Friedreich AtaxiaPhase 3Bambino Gesù — Children's Hospital Rome Italy
Friedreich AtaxiaVatiquinoneBambino Gesù — Research Hospital Rome Italy">Rene Gallegos - Associate Director Clinical Operations MOVE-FA
">Briana Johnson - Manager Clinical Operations PTC743-003e
FRDAN/ATUH Dublin Ireland">Contact
SCA and CANVASrTMSUniversity Hospital Bonn Germany">Contact
MSAi.v. TAK-341DZNE Bonn Germany" style="color: #007acc;">Contact
SCA1, SCA3, HuntingtonASODZNE Bonn Germany">Contact
SCA3Intrathecal ASODZNE Bonn Germany">Contacttrial stopped
Friedreich AtaxiaOmaveloxolonCenter for rare movement disorders Innsbruck Austria">Contact