23 Sep. 2025 | 3 – 4 pm CEST
Zoom Registration
Speaker: Petya Mihaylova & Mary Kearney
Irish Consortium: Tallaght University Hospital and Children’s Health Ireland & FARA Ireland
Disease Group: Leukoencephalopathy
Leriglitazone Trial in Adrenoleukodystrophy
Winter school 2025 “Challenges of treating rare neurological diseases”
12 Mar. 2025
Speaker: Caroline Sevin & Fanny Mochel
Kremlin-Bicêtre University Hospital & La Pitié-Salpêtrière Hospital, Paris, France
Treatment of Metachromatic Leukodystrophies
Winter school 2025 “Challenges of treating rare neurological diseases”
12 Mar. 2025
Speaker: Francesca Fumagalli
IRCCS San Raffaele Scientific Institute, Milan, Italy
State of the art of clinical stage gene therapies for Leukodystrophies
Newborn screening in leukodystrophies
Haematopoietic Stem Cell Transplantation in Leukodystrophies
Krabbe disease – natural history and treatment options
Vanishing white matter
13 Sep. 2022
Speaker: Marjo van der Knaap
VU University Medical Center Amsterdam, Netherlands
Importance of autopsies in leukodystrophies
Measuring disease severity in chronic progressive myelopathy
Pelizaeus-Merzbacher disease and related disorders (pediatric focus)
26 Oct. 2021
Speaker: Nicole Wolf
VU University Medical Center Amsterdam, Netherlands;
Emma Children’s Hospital, Amsterdam, Netherlands
X-Linked leukodystrophies – Update
Adult leukodystrophies/early symptoms of late-onset Leukodystrophies
Metachromatic Leukodystrophy – update
15 Jun. 2021
Speaker: Samuel Gröschel & Ingeborg Krägeloh
University Hospital Tübingen, Germany
MRI pattern recognition in leukodystrophies
8 Jun. 2021
Speaker: Nicole Wolf
VU University Medical Center Amsterdam, Netherlands;
Emma Children’s Hospital, Amsterdam, Netherlands
Treatment of spasticity in HSP and leukodystrophies
6 Oct. 2020
Speaker: Annemieke Buizer & Laura Bonouvrié
VU University Medical Center Amsterdam, Netherlands