20 May 2025 | 3 – 4 pm CEST
Zoom Registration
Speaker: David Bendetowicz
CHU – Reference Center for Rare Multiple System Atrophy, University Hospital Bordeaux, France
Domain: Treatment/Therapy
Speech treatment in Ataxias
Winter school 2025 “Challenges of treating rare neurological diseases”
14 Mar. 2025
Speaker: Adam Vogel
University of Melbourne, Melbourne, Australia
Cognitive and psychiatric treatment in Huntington’s disease
Winter school 2025 “Challenges of treating rare neurological diseases”
14 Mar. 2025
Speaker: Mayke Oosterloo
Maastricht University Medical Center, The Netherlands
Treatment of ataxia – rehabilitation based
Winter school 2025 “Challenges of treating rare neurological diseases”
13 Mar. 2025
Speaker: Gabriella Paparella
IRCCS Eugenio Medea, Institute for rehabilitation medicine, Italy
Treatment of ataxia – genetics based
Winter school 2025 “Challenges of treating rare neurological diseases”
13 Mar. 2025
Speaker: Ronald Buijsen
Leiden University, The Netherlands
Treatment of spasticity in children with rare neurological disorders – who, why, when and what?
Winter school 2025 “Challenges of treating rare neurological diseases”
13 Mar. 2025
Speaker: Annemieke Buizer
Amsterdam UMC, The Netherlands
Disease-modifying treatment approaches/Trials in Huntington disease (HD)
Winter school 2025 “Challenges of treating rare neurological diseases”
12 Mar. 2025
Speaker: Bernhard Landwehrmeyer
University Hospital Ulm, Germany
Treatment of nano-rare neurological diseases
Winter school 2025 “Challenges of treating rare neurological diseases”
12 Mar. 2025
Speaker: Marlen Lauffer
Leiden University Medical Center, The Netherlands
Treatment of Aromatic l-amino acid decarboxylase (AADC) deficiency
Winter school 2025 “Challenges of treating rare neurological diseases”
12 Mar. 2025
Speaker: Thomas Opladen
University Children’s Hospital Heidelberg, Germany
Leriglitazone trial in adrenoleukodystrophy
Winter school 2025 “Challenges of treating rare neurological diseases”
12 Mar. 2025
Speaker: Caroline Sevin & Fanny Mochel
Kremlin-Bicêtre University Hospital & La Pitié-Salpêtrière Hospital, Paris, France
Treatment of metachromatic leukodystrophies
Winter school 2025 “Challenges of treating rare neurological diseases”
12 Mar. 2025
Speaker: Francesca Fumagalli
IRCCS San Raffaele Scientific Institute, Milan, Italy
DBS in Dystonia – the network perspective
Genetic therapies and therapy developments for rare movement disorders
State of the art of clinical stage gene therapies for Leukodystrophies
Huntington disease: new insights into molecular pathogenesis and therapeutic opportunities
Advanced therapies and clinical trials in Leukodystrophies
Haematopoietic Stem Cell Transplantation in Leukodystrophies
Non-pharmacological approaches to treatment in svPPA
Towards precision medicine in NBIA
DBS in Dystonia – Targets, programming and therapeutic challenges
Clinical and genetic predictors of subthalamic nucleus deep brain stimulation in Parkinson’s disease
27 Sep. 2022
Speaker: Daniel Weiß
Hertie Institute for Clinical Brain Research, University of Tübingen, Germany
The logopenic variant of primary progressive aphasia (lvPPA): language, cognitive, neuroradiological issues’
5 Apr. 2022
Speaker: Robert Rusina & Zsolt Cséfalvay
Thomayer Hospital, Prague, Czech Republic; Comenius University in Bratislava, Slovakia
Antisense oligonucleotide mediated exon skipping therapy development for Duchenne muscular dystrophy takes more than an oligonucleotide
ASO RNA splice modulating therapies for genetic brain disorders
Anti-spastic therapies in Hereditary Spastic Paraplegia
11 Jan. 2022
Speaker: Marcondes C. França Jr.
School of Medical Sciences, University Campinas (UNICAMP), Brasil