Publication: “Preparing n-of-1 Antisense Oligonucleotide Treatments for Rare Neurological Diseases in Europe: Genetic, Regulatory, and Ethical Perspectives”

Article: Preparing n-of-1 Antisense Oligonucleotide Treatments for Rare Neurological Diseases in Europe: Genetic, Regulatory, and Ethical Perspectives

Authors: Matthis Synofzik, Willeke M C van Roon-Mom, Georg Marckmann, Hermine A van Duyvenvoorde, Holm Graessner, Rebecca Schüle, Annemieke Aartsma-Rus

Published: September 2021